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Summary

An Open-Label, Long-Term Follow Up Study of Safety and Efficacy in PKU Subjects with PAH Deficiency Previously Administered HMI 102

Conditions

Phenylketonuria, PAH Deficiency

Recruitment Status

ENROLLING_BY_INVITATION

Detailed Description

This Long-Term Follow Up Study will evaluate the safety and efficacy of PKU Subjects with PAH Deficiency Previously Administered HMI 102. Subjects will have already received a single dose of HMI-102 administered intravenously

Eligibility Criteria

Inclusion Criteria:

* Subject was previously administered HMI 102.
* Subject is able to understand the purpose and risks of the study and is willing to provide informed consent.
* Subject is able to comply with all study procedures and long-term follow-up.

Exclusion Criteria:

* Participation in the study is not in the subject's best interest, in the opinion of the Investigator.

Intervention

Intervention Type

Intervention Name

GENETIC

HMI-102

Gender

ALL

Min Age

18 Years

Max Age

55 Years

Download Date

2022-06-30

Principal Investigator

N/A

Primary Contact Information

For more information on this trial, visit clinicaltrials.gov.

Contact

For more information and to contact the study team:

Long-Term Follow Up Study of Subjects Previously Administered HMI 102 NCT04348708