Related Conditions and Treatments Search Start typing a name and the list will filter Conditions Treatments Gene Therapy Treatment Gene therapy is a technique used in an effort to treat or prevent disease. Learn more about Gene Therapy Spinal Muscular Atrophy (SMA) Condition Spinal muscular atrophy is when muscles throughout the body are weakened because nerve cells in the spinal cord and brainstem do not work properly. Learn more about Spinal Muscular Atrophy (SMA) Zolgensma Treatment Zolgensma® (onasemnogene abeparvovec-xioi) is a gene therapy for spinal muscular atrophy (SMA) in children under 2. Learn more about Zolgensma
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