Search Results
Breadcrumb Home Search "The MaP Study": Mapping the Patient Journey in MMA and PA ClinicalTrials.gov ID: NCT03484767 For more information on this trial, visit clinicaltrials.gov . Summary Eligibility Contact Summary Longitudinal, exploratory, natural …
Breadcrumb Home Search A Study to Evaluate the Safety and Efficacy of Long-term Treatment With TEZ/IVA in CF Participants With an F508del CFTR Mutation ClinicalTrials.gov ID: NCT03537651 For more information on this trial, visit clinicaltrials.gov . …
Breadcrumb Home Search Seizure Rescue Medication: Caregiver Education in a Simulation Setting ClinicalTrials.gov ID: NCT03562351 For more information on this trial, visit clinicaltrials.gov . Summary Description Eligibility Intervention Contact Summary 1. …
Breadcrumb Home Search ATHN 7: Hemophilia Natural History Study ClinicalTrials.gov ID: NCT03619863 For more information on this trial, visit clinicaltrials.gov . Summary Description Eligibility Contact Summary This is a real-world study of the safety of …
Breadcrumb Home Search JASPER Intervention in Down Syndrome ClinicalTrials.gov ID: NCT03653143 For more information on this trial, visit clinicaltrials.gov . Summary Eligibility Intervention Contact Summary The goal of this study is to determine whether …
Breadcrumb Home Search Evaluation of VX 445/TEZ/IVA in Cystic Fibrosis Subjects 6 Through 11 Years of Age ClinicalTrials.gov ID: NCT03691779 For more information on this trial, visit clinicaltrials.gov . Summary Eligibility Intervention Contact Summary …
Breadcrumb Home Search A Multicenter, Open-label, Pilot Study of Soticlestat (TAK-935/OV935) in Participants With 15Q Duplication Syndrome (Dup 15q) or Cyclin-Dependent Kinase-Like 5 (CDKL5) Deficiency Disorder (ARCADE STUDY) ClinicalTrials.gov ID: …
Breadcrumb Home Search Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy ClinicalTrials.gov ID: NCT03703882 For more information on this trial, visit clinicaltrials.gov . Summary Description Eligibility Intervention Contact Summary …
Breadcrumb Home Search Type 1 Diabetes Management Using a Very Low Carbohydrate Versus Standard Diet ClinicalTrials.gov ID: NCT03710928 For more information on this trial, visit clinicaltrials.gov . Summary Eligibility Intervention Contact Summary Despite …
Breadcrumb Home Search M6620 (VX-970) in Selected Solid Tumors ClinicalTrials.gov ID: NCT03718091 For more information on this trial, visit clinicaltrials.gov . Summary Description Eligibility Intervention Contact Summary This research study is studying a …