Sickle Cell Disease Program | Gene therapy for sickle cell disease: The journey to a new treatment

Discover how groundbreaking research at Boston Children’s Hospital has led to a new gene therapy for sickle cell disease. Hear from Stu Orkin, MD, Dan Bauer, MD, David Williams, MD, and others as they discuss the significance of this FDA-approved treatment for the sickle cell community. Boston Children’s is proud to be recognized as a center of excellence for multiple gene therapies, including those for sickle cell disease.